AAV-tRNA-sgRNA-CMV-hAsCpf1 Ready to Package
Adeno-associated Virus (AAV) - 14. page
AAV-EF1a-FRT-mCherry-WPRE and AAV-CAG-FRT-GFP-WPRE Ready to Package
AAV-EF1a-FRT-mCherry-WPRE and AAV-CAG-FRT-GFP-WPRE Ready to Package
AAV-CMV-SpCas9-HF1 (Cas9 High-fidelity Version) Ready to Package
AAV-CMV-SpCas9-HF1 (Cas9 High-fidelity Version) Ready to Package
Effective delivery of large genes to the retina by dual AAV vectors
Retinal gene therapy with adeno-associated viral (AAV) vectors is safe and effective in humans. However, AAV’s limited cargo capacity prevents its application to therapies of inherited retinal diseases due to […]
AAV-CMV-OptoSTIM1 Ready to Package
AAV-CMV-OptoSTIM1 Ready to Package
AAV-CMV-pHuji Ready to Package
AAV-CMV-pHuji Ready to Package
AAV-CMV-saCas9-U6-sgRNA(Scramble) Ready to Package
AAV-CMV-saCas9-U6-sgRNA(Scramble) Ready to Package
AAV-EF1a-DIO-hChR2(H134R)-YFP-WPRE Ready to Package
AAV-EF1a-DIO-hChR2(H134R)-YFP-WPRE Ready to Package
AAV-mediated gene delivery of BDNF or GDNF is neuroprotective in a model of Huntington disease.
Huntington disease (HD) is a neurodegenerative disorder that results in the progressive loss of GABAergic medium spiny projection neurons in the striatum. Neurotrophic factors have demonstrated neuroprotective actions on striatal […]