ATGCTGGCGACTCAGAGTCAGTTCCAGACCCTCAACCTCTCGGAGAACCTCCAGCAGCGCCCTCTGGTGTGGGACCTAATACAATGGCTGCAGGCGGTGGCGCAC CAATGGCAGACAATAACGAAGGCGCCGACGGAGTGGGTAGTTCCTCGGGAAATTGGCATTGCGATTCCACATGGCTGGGCGACAGAGTCATCACCACCAGCACC CGAACCTGGGCCCTGCCCACCTACAACAACCACCTCTACAAGCAAATCTCCAACGGGACATCGGGAGGAGCCACCAACGACAACACCTACTTCGGCTACAGCAC CCCCTGGGGGTATTTTGACTTTAACAGATTCCACTGCCACTTTTCACCACGTGACTGGCAGCGACTCATCAACAACAACTGGGGATTCCGGCCCAAGAGACTCAG CTTCAAGCTCTTCAACATCCAGGTCAAGGAGGTCACGCAGAATGAAGGCACCAAGACCATCGCCAATAACCTCACCAGCACCATCCAGGTGTTTACGGACTCGGA GTACCAGCTGCCGTACGTTCTCGGCTCTGCCCACCAGGGCTGCCTGCCTCCGTTCCCGGCGGACGTGTTCATGA
Sequence of AAV5 Assembly-Activating Protein (AAP)
atgctggacccagcggatcccagcagctgcaaatcccagcccaaccagcctcaagtttgggagctgatacaatgtctgcgggaggtggcggcccattgggcgacaataaccaaggtgccgatgg agtgggcaatgcctcgggagattggcattgcgattccacgtggatgggggacagagtcgtcaccaagtccacccgaacctgggtgctgcccagctacaacaaccaccagtaccgagagatcaaa agcggctccgtcgacggaagcaacgccaacgcctactttggatacagcaccccctgggggtactttgactttaaccgcttccacagccactggagcccccgagactggcaaagactcatcaacaact actggggcttcagaccccggtccctcagagtcaaaatcttcaacattcaagtcaaagaggtcacggtgcaggactccaccaccaccatcgccaacaacctcacctccaccgtccaagtgtttacggac gacgactaccagctgccctacgtcgtcggcaacgggaccgagggatgcctgccggccttccctccgcaggtctttacgctgccgcagtacggttacgcgacgctga
Sequence of AAV2 Assembly-Activating Protein (AAP)
atgctggagacgcagactcagtacctgacccccagcctctcggacagccaccagcagccccctctggtctgggaactaatacgatggctacaggcagtggcgcaccaatggcagacaataacga gggcgccgacggagtgggtaattcctcgggaaattggcattgcgattccacatggatgggcgacagagtcatcaccaccagcacccgaacctgggccctgcccacctacaacaaccacctctac aaacaaatttccagccaatcaggagcctcgaacgacaatcactactttggctacagcaccccttgggggtattttgacttcaacagattccactgccacttttcaccacgtgactggcaaagactc atcaacaacaactggggattccgacccaagagactcaacttcaagctctttaacattcaagtcaaagaggtcacgcagaatgacggtacgacgacgattgccaataaccttaccagcacggtt caggtgtttactgactcggagtaccagctcccgtacgtcctcggctcggcgcatcaaggatgcctcccgccgttcccagcagacgtcttcatggtgccacagtatggatacctcaccctga
Validated Target Region against Mouse Lamtor1
CGTATGCCTATAGTGCACTTT
Two Validated Target Regions against Mouse ROCK2
CAGAAGCGTTGTCTTATGCAA TTGGATAAACATGGACATCTA
Two validated target regions
N-Taf : CTCAGGCTAAGCCTCCTGATT C/N-Taf: TGGAGGAAGCAGAATTAGAAA
Validated Target Region against Mouse Rock2
5’-CAGAAGCGTTGTCTTATGCAA-3’ 5’-TTGGATAAACATGGACATCTA-3’
Human VMD2 Promoter
AATTC TGTCATTTTA CTAGGGTGAT GAAATTCCCA AGCAACACCATCCTTTTCAG ATAAGG GCAC TGAGGCTGAG AGAGGAGCTG AAACCTACCC GGCGTCACCACACACAGGTG GCAAG GCTGG GACCAGAAAC CAGGACTGTT GACTGCAGCC CGGTATTCATTCTTTCCATA GCCCA CAGGG CTGTCAAAGA CCCCAGGGCC TAGTCAGAGG CTCCTCCTTCCTGGAGAGTT CCTGG CACAG AAGTTGAAGC TCAGCACAGC CCCCTAACCC CCAACTCTCTCTGCAAGGCC TCAGG […]